REGENXBIO Inc., a clinical-stage biotechnology company, provides gene therapies that deliver functional genes to cells with genetic defects in the United States. Its gene therapy product candidates are based on NAV Technology Platform, a proprietary adeno-associated virus gene delivery platform. The company’s products in pipeline includes ABBV-RGX-314 for the treatment of wet age-related macular degeneration, diabetic retinopathy, and other chronic retinal diseases; and RGX-202, which is in Phase III clinical trial for the treatment of Duchenne muscular dystrophy, as well as RGX-121 for the treatment of mucopolysaccharidosis type II. It also develops RGX-111 for the treatment of mucopolysaccharidosis type I, RGX-181 for the treatment of late-infantile neuronal ceroid lipofuscinosis type 2, and RGX-381 for the treatment of the ocular manifestations of CLN2 disease. In addition, the company licenses its NAV Technology Platform to other biotechnology and pharmaceutical companies. Further, it has a collaboration and license agreement with AbbVie Global Enterprises Ltd. to develop ABBV-RGX-314 outside the United States. REGENXBIO Inc. was incorporated in 2008 and is headquartered in Rockville, Maryland.
Gene Therapy Pionee | REGENXBIO's innovative pipeline targets genetic and rare diseases, with promising developments in DMD and ocular therapies positioning it for potential market leadership |
Financial Prospects | Analysts project stock upside with price targets ranging from $18 to $52, despite current market challenges and negative near-term EPS estimates |
Competitive Edge | Explore REGENXBIO's differentiated DMD treatment, addressing limitations of existing therapies and potentially capturing a significant share of the $3 billion market |
Strategic Catalysts | Upcoming milestones include potential $200M payment for DR trial initiation and BLA submissions, with opportunities for accelerated regulatory pathways |
Metrics to compare | RGNX | Sector Sector - Average of metrics from a broad group of related Healthcare sector companies | Relationship RelationshipRGNXPeersSector | |
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P/E Ratio | −1.9x | −3.6x | −0.5x | |
PEG Ratio | −0.08 | −0.09 | 0.00 | |
Price/Book | 1.7x | 2.1x | 2.6x | |
Price / LTM Sales | 5.3x | 10.4x | 2.9x | |
Upside (Analyst Target) | 249.6% | 245.4% | 57.2% | |
Fair Value Upside | Unlock | 9.5% | 8.9% | Unlock |