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BioMarin Pharmaceutical Inc. engages in the development and commercialization of therapies for people with serious and life-threatening rare diseases and medical conditions. Its commercial products include Vimizim, an enzyme replacement therapy for the treatment of mucopolysaccharidosis (MPS) IV type A, a lysosomal storage disorder; Naglazyme, a recombinant form of N-acetylgalactosamine 4-sulfatase for patients with MPS VI; and Kuvan, a proprietary synthetic oral form of 6R-BH4 that is used to treat patients with phenylketonuria (PKU), an inherited metabolic disease. The company’s commercial products also comprise Palynziq, a PEGylated recombinant phenylalanine ammonia lyase enzyme, which is delivered through subcutaneous injection to reduce blood Phe concentrations; Brineura, a recombinant human tripeptidyl peptidase 1 for the treatment of patients with ceroid lipofuscinosis type 2, a form of Batten disease; Voxzogo, a once daily injection analog of c-type natriuretic peptide for the treatment of achondroplasia; and Aldurazyme, a purified protein designed to be identical to a naturally occurring form of the human enzyme alpha-L-iduronidase. In addition, it develops Roctavian, an adeno associated virus vector, for the treatment of patients with severe hemophilia A. The company serves specialty pharmacies, hospitals, and non-U.S. government agencies, as well as distributors and pharmaceutical wholesalers in the United States, Europe, Latin America, and internationally. It has license and collaboration agreements with Sarepta Therapeutics; Ares Trading S.A.; Catalyst Pharmaceutical Partners, Inc.; and CAMP4 Therapeutics Corporation. The company was incorporated in 1996 and is headquartered in San Rafael, California.
Rare Disease Pionee | BioMarin leads in rare genetic disease therapies, with a robust portfolio and strategic focus on high-potential drugs like Voxzogo and Roctavian |
Financial Fortitude | Strong Q2 2024 performance drives raised revenue guidance to $2.75-2.83B, with ambitious plans to achieve 40%+ operating margins mid-term |
Voxzogo's Ascent | Explore Voxzogo's exceptional growth trajectory, with analysts projecting peak sales of $2.4B by 2032 and potential label expansions |
Analyst Optimism | Wall Street bullish on BioMarin, with price targets ranging from $89 to $115, reflecting confidence in the company's growth strategy and pipeline |
Metrics to compare | BMRN | Sector Sector - Average of metrics from a broad group of related Healthcare sector companies | Relationship RelationshipBMRNPeersSector | |
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P/E Ratio | 37.7x | −2.8x | −0.6x | |
PEG Ratio | 0.32 | −0.16 | 0.00 | |
Price/Book | 2.2x | 2.1x | 2.6x | |
Price / LTM Sales | 4.4x | 2.8x | 3.1x | |
Upside (Analyst Target) | 46.0% | 29.4% | 55.2% | |
Fair Value Upside | Unlock | 16.4% | 9.8% | Unlock |